EM2510C "Targeting BMP, Activin, and TGF Beta Signaling in Pulmonary Hypertension: Lessons from Human Genetics, Disease Models and Clinical Trials" (IM GR-101025)
Purpose and Overview
This seminar discusses the rationale for the development of several novel therapies, including the Activin Signaling Inhibitor (ASI) drug class, that target activin, GDF, BMP and TGF-beta signaling for the treatment of pulmonary arterial hypertension (PAH). These programs were informed by human genetics, signaling biology, biomarkers of disease, and experimental models. The early experience from these trials has raised questions about the potential mechanisms of therapeutic and adverse effects of these therapies.
Target Audience
UT Southwestern faculty, fellows, residents and medical students, community physicians, nurse clinicians, physician assistants and nurses.
Learning Objectives
At the conclusion of this activity, the participant should be able to:
- Identify syndromic or genetic versus non-syndromic pulmonary arterial hypertension syndromes.
- Understand the rationale for correcting aberrant activin and BMP signaling in PAH as a paradigm for treating PAH.
- Recognize potential adverse events related to the use of Activin Signaling Inhibitors such as sotatercept.

Paul B. Yu, M.D., Ph.D.
Associate Professor of Medicine
Division of Cardiology
Director, MGH Cardiovascular Research Center
Massachusetts General Hospital and Harvard Medical School
Available Credit
- 1.00 AMA
Price
Required Hardware/software
Activities should be run with recent versions of common browsers, including Internet Explorer, Firefox and Google Chrome

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